StevenWPipeMD

PubMed

• Corticosteroid use to mitigate transaminitis-associated decline in FVIII levels following valoctocogene roxaparvovec gene therapy: clinical practice guidance.
  Barbara A Konkle, Flora Peyvandi, Graham R Foster, Cedric Hermans, Vincenzo La Mura
  Journal of Thrombosis and Haemostasis. 2025-03-14
• Long-term safety and efficacy of fitusiran prophylaxis, and perioperative management, in people with hemophilia A or B.
  Steven W Pipe, Toshko Lissitchkov, Pencho Georgiev, Sarah Mangles, Inga Hegemann
  Blood Advances. 2025-03-11
• Haemophilia.
  Pratima Chowdary, Manuel Carcao, Gili Kenet, Steven W Pipe
  Lancet. 2025-03-01

Abstracts/Posters

• One Year Data from a Phase 2b Trial of AMT-061 (AAV5-Padua hFIX variant), an Enhanced Vector for Gene Transfer in Adults with Severe or Moderate-Severe Hemophilia B
  Steven Pipe, 61st Annual American Society of Hematology Meeting, Orlando, FL, 12/8/2019

Lectures

• Moving Beyond Factor: Shifting the Paradigm in Hemophilia Through Gene Therapy 
  61st Annual American Society of Hematology Meeting - Orlando, FL - 12/7/2019
• Fitusiran, an RNAi Therapeutic Targeting Antithrombin to Restore Hemostatic Balance in Patients with Hemophilia a or B with or without Inhibitors: Management of Acute ... 
  61st Annual American Society of Hematology Meeting - Orlando, FL - 12/7/2019
• First-in-human Gene Therapy Study of AAVhu37 Capsid Vector Technology in Severe Hemophilia A 
  61st Annual American Society of Hematology Meeting - Orlando, FL - 12/7/2019