OzlemGoker-AlpanMD

Clinical Trials

• Safety and Efficacy Study of Several Replagal Dosing Regimens on Cardiac Function in Adults With Fabry Disease Start of enrollment: 2008 Dec 29

  Completed

  Phase 3

• Treatment Protocol of Replagal for Patients With Fabry Disease

  No longer available

• Exploration of Immunity in Gaucher Disease Start of enrollment: 2011 Apr 01

  Completed

• Pregnancy and Birth Outcome in Women With Pompe Disease Start of enrollment: 2012 Feb 01

  Completed

• Molecular and Cellular Mechanisms of Lysosomal Storage Diseases Start of enrollment: 2013 Nov 01

  Recruiting

• Open-Label Extension Study of the Long-Term Effects of Migalastat HCL in Patients With Fabry Disease Start of enrollment: 2015 Mar 14

  Completed

  Phase 3

• First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221 Start of enrollment: 2016 Jan 01

  Active, not recruiting

  Phase 1, Phase 2

• Biomarker Analysis for GBA Associated Parkinson's Disease Start of enrollment: 2018 Feb 01

  Recruiting

• Screening of Lysosomal Storage Disorders Diseases in Minority Groups Start of enrollment: 2016 Mar 17

  Active, not recruiting

• Cellular Pharmacodynamics of Small Molecules in Lysosomal Storage Disorders Start of enrollment: 2018 Jul 06

  Recruiting

• Immune Biomarkers Related to Bone Pathology in Patients With Type 1 Gaucher Disease Start of enrollment: 2019 May 15

  Recruiting

• Assess Urine Biomarkers to Predict Nephropathy in Fabry Disease Start of enrollment: 2023 Sep 14

  Recruiting

  Roles: Principal Investigator, Contact

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