Ami Jayant Shah MD

Pediatric Hematology & Oncology•Palo Alto, CA

Pediatric Hematologic Oncology

Professor of Clinical Pediatrics, Stanford University

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725 Welch RdPalo Alto, CA 94304
Phone+1 650-497-8000
Fax+1 650-497-8959

Education & Training

Children's Hospital Los AngelesFellowship, Pediatric Hematology/Oncology, 1993 - 1996
Children's Hospital Los AngelesResidency, Pediatrics, 1990 - 1993
University of North Carolina at Chapel Hill School of MedicineClass of 1990

Certifications & Licensure

CA State Medical License 1991 - 2026
TX State Medical License 1997 - 2000
American Board of Pediatrics Pediatric Hematology-Oncology

Awards, Honors, & Recognition

CMS Meaningful Use Stage 1 Certification EpicCare Ambulatory EMR, Epic Systems Corporation, 2013

Clinical Trials

Autologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Lentiviral Vector Encoding for the Human ADA Gene Start of enrollment: 2013 Aug 02
Completed
Phase 1, Phase 2
Gene Therapy for Pyruvate Kinase Deficiency (PKD) Start of enrollment: 2020 Jul 06
Active, not recruiting
Phase 1
Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease Start of enrollment: 2022 Aug 02
RECRUITING
PHASE3
A Long-term Follow-up Study in Participants Who Received CTX001 Start of enrollment: 2021 Jan 20
ENROLLING_BY_INVITATION
PHASE3
Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product Start of enrollment: 2016 Jan 22
ACTIVE_NOT_RECRUITING
A Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy (CALD) Start of enrollment: 2019 Jan 24
Completed
Phase 3
Patients Treated for Wiskott-Aldrich Syndrome (WAS) Since 1990 Start of enrollment: 2014 Feb 02
Completed
Patients Treated for SCID (1968-Present) Start of enrollment: 2011 May 15
Enrolling by invitation
Patients Treated for Chronic Granulomatous Disease (CGD) Since 1995 Start of enrollment: 2014 Jun 01
Enrolling by invitation
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Publications & Presentations

PubMed

23 citations
Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia.
Franco Locatelli, Peter Lang, Donna Wall, Roland Meisel, Selim Corbacioglu
The New England Journal of Medicine. 2024-05-09
31 citations
Exagamglogene Autotemcel for Severe Sickle Cell Disease.
Haydar Frangoul, Franco Locatelli, Akshay Sharma, Monica Bhatia, Markus Mapara
The New England Journal of Medicine. 2024-05-09
1 citations
Diagnosis and management of pyruvate kinase deficiency: international expert guidelines.
Hanny Al-Samkari, Nadine Shehata, Kelly Lang-Robertson, Paola Bianchi, Andreas Glenthøj
The Lancet. Haematology. 2024-03-01

Professional Memberships

American Society of Hematology - ASH
Member
American Society of Blood and Marrow Transplantation
Member
Society of Pediatric Research
Member
American Society of Pediatric Hematology Oncology
Member